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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, achondroplasia, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hereditary endocrine growth disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaRecruitingPhase 22026-07-13NCT07169279

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OrganizationsLinked trials
QED Therapeutics, a BridgeBio company5

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