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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular DystrophyDuchene Muscular DystrophyRecruitingPhase 2 / Phase 32026-10-02NCT07856329
Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative ColitisDigestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisActive, not recruitingPhase 32026-08-03NCT04624230
Efficacy, Safety & Utilisation of Nuwiq, Octanate and Wilate in Previously Untreated & Minimally Treated Haemophilia A PatientsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingNot stated2026-06-02NCT03695978
A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical PracticeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, Respiration Disorders, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, limb-girdle muscular dystrophy, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, respiratory system disorder, sarcoglycanopathyActive, not recruitingNot stated2025-11-06NCT04475926
Transmural Care for Chronically Ill Children: Scientific Guidance and Evaluation of Pilot ProjectsChronic Disease, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and SymptomsEnrolling by invitationNot stated2024-11-07NCT06679595
Registry on Obesity Surgery in AdolescentsAdolescent Obesity, Body Weight, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Pediatric Obesity, Signs and Symptoms, morbid obesity, nutritional disorder, obesity disorder, overnutritionNot yet recruitingNot stated2019-02-12NCT03203161