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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical PracticeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, Respiration Disorders, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, limb-girdle muscular dystrophy, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, respiratory system disorder, sarcoglycanopathyActive, not recruitingNot stated2025-11-06NCT04475926

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OrganizationsLinked trials
Sarepta Therapeutics, Inc.15

26 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Anne & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States1
Arkansas Children'sLittle RockUnited States7
Azienda Ospedale Università PadovaPadovaItaly1
Barrow Neurological InstitutePhoenixUnited States50
Children's Hospital - London Health Science CentreLondonCanada1
Children's Hospital of The King's DaughtersNorfolkUnited States87
Fondazione IRCCS Ca' Granda Ospedale Maggiore PoliclinicoMilanItaly44
Hospital de Clinicas de Porto Alegre (HCPA) - PPDSPorto AlegreBrazil5
Hospital Sant Joan de Déu Universidad de BarcelonaBarcelonaSpain1
Hôpital Universitaire des Enfants Reine FabiolaBrusselsBelgium6
Institute of Genetic Medicine, International Centre for LifeNewcastle upon TyneUnited Kingdom1
Istituto Giannina GasliniGenoaItaly1
Karolinska Universitetssjukhuset SolnaStockholmSweden2
Lokman Hekim Etlik HastanesiAnkaraTurkey (Türkiye)1
Nationwide Children's HospitalColumbusUnited States309
Oregon Health and Science UniversityPortlandUnited States1
The Children's Hospital of PhiladelphiaPhiladelphiaUnited States62
UCL Institute of Child Health & Great Ormond Street Hospital for ChildrenLondonUnited Kingdom1
University Hospital GentGhentBelgium2
University of California San DiegoLa JollaUnited States39
University of California, Davis Health Dept of PM&RSacramentoUnited States1
University of Texas Southwestern Medical CenterDallasUnited States2
University of Utah HospitalSalt Lake CityUnited States4
Universitätsklinikum EssenEssenGermany1
UZ LeuvenLeuvenBelgium9