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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Dose Escalation Study of CLR 131 in Pediatric Relapsed/Refractory Malignant Tumors Including Neuroblastoma and SarcomasCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Ewing sarcoma, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Hodgkins lymphoma, Male Urogenital Diseases, Myosarcoma, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, Neuroectodermal Tumors, Primitive, Peripheral, Urogenital Diseases, Urogenital Neoplasms, Wilms tumor, astrocytoma (excluding glioblastoma), benign urinary system neoplasm, brain disorder, brainstem cancer, central nervous system cancer, central nervous system disorder, connective tissue neoplasm, desmoplastic small round cell tumor, diffuse intrinsic pontine glioma, ependymoma, epithelial neoplasm, glioblastoma, glioma, gliosarcoma, hereditary disease, hereditary neoplastic syndrome, immune system disorder, immunoproliferative disorder, kidney cancer, kidney disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, medulloblastoma, mixed neoplasm, myomatous neoplasm, neoplasm, nervous system disorder, neuroblastoma, neuroepithelial neoplasm, osteosarcoma, pediatric lymphoma, primitive neuroectodermal tumor, rhabdoid tumor, rhabdomyosarcoma, sarcoma, synovial sarcoma, urinary system disorderActive, not recruitingPhase 12026-10-01NCT03478462
A Study to Assess the Incidence of Skin Cancers in Patients With Epidermolysis Bullosa Receiving FilsuvezCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, junctional epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-09-28NCT06423573
BEATRIX: A Study to Learn About a Group B Streptococcus Vaccine in Healthy Pregnant Women and Their BabiesHealthyRecruitingPhase 32026-09-25NCT07160244
A Study Investigating Oral Ozanimod (RPC1063) in Pediatric Participants With Moderate to Severe Active Ulcerative ColitisDigestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisRecruitingPhase 2 / Phase 32026-09-24NCT05076175
Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)Abnormalities, Multiple, Arrhythmias, Cardiac, COVID-19, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronaviridae Infections, Down syndrome, Dyssomnias, Edema, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Hemic and Lymphatic Diseases, Hemorrhage, Infant, Newborn, Diseases, Infant, Premature, Diseases, Infections, Inflammation, Kawasaki disease, Lung Injury, Menorrhagia, Menstruation Disturbances, Neurobehavioral Manifestations, Neurologic Manifestations, Nidovirales infectious disease, Nutritional and Metabolic Diseases, Orthocoronavirinae infectious disease, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, Signs and Symptoms, Skin and Connective Tissue Diseases, Sleep Disorders, Intrinsic, Suppuration, Urogenital Diseases, Uterine Hemorrhage, Ventilator-Induced Lung Injury, Water-Electrolyte Imbalance, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, attention deficit hyperactivity disorder, inattentive type, blood coagulation disease, bronchopulmonary dysplasia, cardiovascular disorder, cellulitis, chromosomal disorder, coagulation protein disease, connective tissue disorder, endocrine system disorder, female reproductive system disorder, heart disorder, heart failure, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, hyperaldosteronism, hyperphosphatemia, hypertensive disorder, inherited blood coagulation disorder, insomnia, intellectual disability, lung disorder, lymphatic system disorder, metabolic disease, nervous system disorder, neurodevelopmental disorder, oppositional defiant disorder, pediatric multisystem inflammatory disease, COVID-19 related, phosphorus metabolism disease, pneumonia, potassium deficiency disease, primary aldosteronism, psychiatric disorder, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, respiratory tract infectious disorder, skin disorder, skin disorder caused by infection, skin infection, skin vascular disease, sleep-wake disorder, uterine disorder, vascular disorder, vascular hemostatic disease, vasculitis, viral infectious disease, viral pneumoniaRecruitingNot stated2026-08-21NCT04278404
A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Alectinib in Pediatric Participants With ALK Fusion-Positive Solid or CNS TumorsNeoplasms by Site, central nervous system cancer, neoplasm, nervous system disorderActive, not recruitingPhase 1 / Phase 22026-08-14NCT04774718
TReatment for ImmUne Mediated PathopHysiologyBrain Diseases, Metabolic, Digestive System Diseases, Hepatic Insufficiency, Nutritional and Metabolic Diseases, acute liver failure, brain disorder, central nervous system disorder, hepatic encephalopathy, liver disorder, liver failure, metabolic disease, nervous system disorderActive, not recruitingPhase 22026-08-12NCT04862221
A Long-term Follow-up Study in Participants Who Received CTX001Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemiaEnrolling by invitationPhase 32026-08-11NCT04208529
Multicenter Trial of ECMO in Children With Severe Cardiac Failure Using the Cardiohelp SystemCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infarction, Necrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Shock, Shock, Cardiogenic, cardiomyopathy, cardiovascular disorder, congenital heart disease, heart disorder, heart failure, ischemic disease, myocardial infarction, myocardial ischemia, vascular disorderRecruitingPhase 22026-08-10NCT06080074
A Study of CC-97540 (BMS-986353 or Zola-cel), CD19-Targeted NEX-T CAR T Cells, in Participants With Active SLE Despite Immunosuppressants (Breakfree-SLE)Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Skin and Connective Tissue Diseases, Urogenital Diseases, autoimmune disease, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, lupus nephritis, nephritis, systemic lupus erythematosus, urinary system disorderActive, not recruitingPhase 22026-08-03NCT07015983
Beeline: A Phase 3 Study in GRIN-related Neurodevelopmental DisorderGRIN-related complex neurodevelopmental disorderRecruitingPhase 32026-07-17NCT07224581
A Long-Term Safety Follow-up Registry for Patients Who Received Treatment With Prademagene Zamikeracel for Recessive Dystrophic Epidermolysis Bullosa (RDEB) in the Post-Marketing SettingCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-07-14NCT07700966
Trial of Indication-Based Transfusion of Red Blood Cells in ECMOPathologic Processes, Pathological Conditions, Signs and Symptoms, Shock, multiple organ dysfunction syndromeActive, not recruitingNot applicable2026-07-02NCT05405426
Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 1 / Phase 22026-07-02NCT04819841
Virtual Reality-enhanced Psychotherapy for Perinatal Depressiondepressive disorderEnrolling by invitationNot applicable2026-04-06NCT07279311
Studying Melatonin and Recovery in TeensAcute Pain, Chronic Pain, Kyphosis, Neurologic Manifestations, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Postoperative Pain, Signs and Symptoms, Spinal Curvatures, bone disorder, musculoskeletal system disorder, scoliosis, spondylolisthesis, spondylolysis, spondylosis, vertebral column disorderRecruitingNot applicable2026-03-18NCT06093477
Supraglottic Airway for Resuscitation TrialDelivery Room Resuscitation; Implementation Research; Infant, Newborn; Laryngeal Mask Airways; Neonatal Resuscitation; Positive Pressure Ventilation; Supraglottic AirwayRecruitingNot applicable2026-02-27NCT07150923
Finger Plethysmography to Predict Fluid Responsiveness in Healthy Pregnancy and Severe PreeclampsiaFemale Urogenital Diseases and Pregnancy Complications, Urogenital Diseases, hypertension, pregnancy-induced, preeclampsia, pregnancy disorderNot yet recruitingNot stated2026-02-24NCT07430254
Impact of Patient Choice for Epidural Potency on Maternal SatisfactionEpidural Analgesia, Obstetric; Maternal SatisfactionNot yet recruitingNot applicable2026-02-17NCT07414407
Study of Lurbinectedin Monotherapy in Pediatric and Young Adult Participants With Relapsed/Refractory Ewing SarcomaEwing sarcoma, Neoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, neoplasm, osteosarcoma, sarcomaRecruitingPhase 1 / Phase 22026-02-03NCT05734066
Social & Contextual Impact on Children Undergoing Liver TransplantationDigestive System Diseases, liver disorderActive, not recruitingNot stated2026-01-26NCT04551742
Follow-up Automatically vs. As-Needed Comparison (FAAN-C) TrialDigestive System Diseases, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Infections, Male Urogenital Diseases, Soft Tissue Infections, Urogenital Diseases, digestive system disorder, gastroenteritis, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, urinary system disorder, urinary tract infectionRecruitingNot applicable2025-12-10NCT05471908
Oral Pyridoxal 5'-Phosphate for the Treatment of Patients With PNPO DeficiencyPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyRecruitingPhase 32025-10-16NCT04706013
Viral Specific T-Lymphocytes to Treat Infection With Adenovirus, Cytomegalovirus or Epstein-Barr Virus in Patients With Compromised ImmunityDNA Virus Infections, Epstein-Barr virus infection, Herpesviridae infectious disease, Infections, Tumor Virus Infections, adenoviridae infectious disease, cytomegalovirus infection, viral infectious diseaseRecruitingPhase 1 / Phase 22025-08-14NCT06909110