UC San Francisco
UC San Francisco
San Francisco, California, United States2 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis | eye disorder, retinal degeneration, retinal disorder, retinoschisis | Recruiting | Phase 3 | 2026-09-29 | NCT05878860 | |
| The REPLACE Registry for Cholbam® (Cholic Acid) | Abnormalities, Multiple, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Peroxisomal Disorders, Urogenital Diseases, Zellweger spectrum disorders, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of bile acid synthesis, inborn errors of metabolism, kidney disorder, liver disorder, metabolic disease, nervous system disorder, urinary system disorder | Active, not recruiting | Not stated | 2026-07-31 | NCT03115086 |