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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
The REPLACE Registry for Cholbam® (Cholic Acid)Abnormalities, Multiple, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Peroxisomal Disorders, Urogenital Diseases, Zellweger spectrum disorders, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of bile acid synthesis, inborn errors of metabolism, kidney disorder, liver disorder, metabolic disease, nervous system disorder, urinary system disorderActive, not recruitingNot stated2026-07-31NCT03115086

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OrganizationsLinked trials
Mirum Pharmaceuticals, Inc.15

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Research sitesCityCountryLinked trials
Children's Center For Digestive HealthAtlantaUnited States1
Children's Healthcare of AtlantaAtlantaUnited States38
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Golisano Children's Hospital, URMCRochesterUnited States1
Icahn School of Medicine at Mount SinaiNew YorkUnited States342
Kidz Pediatric Multispecialty GroupHollywoodUnited States1
Mayo ClinicRochesterUnited States68
Monroe-Carell Jr. Children's Hospital at VanderbiltNashvilleUnited States1
Montefiore Medical CenterNew YorkUnited States1
Nemours duPont Pediatrics Specialty ClinicJacksonvilleUnited States1
Nicklaus Children's HospitalMiamiUnited States112
NYU Langone - NYU Grossman School of MedicineNew YorkUnited States3
Ochsner Hospital for ChildrenNew OrleansUnited States1
Office of Dr. Esperanza Font-Montgomery MDColumbiaUnited States1
Primary Children's HospitalSalt Lake CityUnited States111
Stanford School of MedicinePalo AltoUnited States1
The Children's Hospital of PhiladelphiaPhiladelphiaUnited States62
The Community Health ClinicTopekaUnited States1
UC San FranciscoSan FranciscoUnited States2
UNC Chapel HillChapel HillUnited States12
University of Alabama BirminghamBirminghamUnited States16
University of MinnesotaMinneapolisUnited States30
University of OklahomaOklahoma CityUnited States28
Washington University at St LouisSt LouisUnited States1