23 results · Page 1 of 1

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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study Assessing the Efficacy, Safety and PK of Alpelisib (BYL719) in Pediatric and Adult Patients With PIK3CA-related Overgrowth SpectrumPIK3CA-related Overgrowth Spectrum (PROS)Active, not recruitingPhase 22026-10-07NCT04589650
A Study of Nipocalimab or Intravenous Immunoglobulin (IVIG) in Pregnancies At Risk of Fetal and Neonatal Alloimmune Thrombocytopenia (FNAIT)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, blood platelet disease, hematologic disorder, neonatal thrombocytopenia, thrombocytopeniaRecruitingPhase 32026-09-25NCT06533098
A Study of Nipocalimab in Pregnancies at Risk for Severe Hemolytic Disease of the Fetus and Newborn (HDFN)Hemolytic Disease of the Fetus and NewbornRecruitingPhase 32026-09-25NCT05912517
A Study of Selexipag as Add-On Treatment to Standard of Care in Children With Pulmonary Arterial Hypertensioncardiovascular disorder, hypertensive disorder, lung disorder, pulmonary hypertension, respiratory system disorder, vascular disorderActive, not recruitingPhase 32026-09-25NCT04175600
Efficacy and Safety of Erenumab in Pediatric Participants With Episodic MigraineHeadache, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, headache disorder, hypnic headache, migraine disorder, nervous system disorderActive, not recruitingPhase 32026-09-21NCT03836040
Study to Assess the Efficacy, Pharmacokinetics, Safety and Tolerability of Iptacopan in Pediatric Patients With Primary IgANFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, IgA glomerulonephritis, Male Urogenital Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urination Disorders, Urogenital Diseases, Urological Manifestations, autoimmune disease, glomerulonephritis, immune system disorder, kidney disorder, nephritis, proteinuria, urinary system disorderRecruitingPhase 32026-09-09NCT06994845
Open-Label, Long-Term, Extension Study of Infigratinib in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 22026-08-26NCT07393373
Study of Efficacy and Safety of Tisagenlecleucel in HR B-ALL EOC MRD Positive PatientsB-cell acute lymphoblastic leukemia, B-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasm, Residual, Neoplasms by Histologic Type, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Tumor Virus Infections, immune system disorder, immunoproliferative disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, viral infectious diseaseActive, not recruitingPhase 22026-08-19NCT03876769
A U.S. Registry of Eosinophilic Esophagitis Pediatric, Adolescent and Adult Patients Treated With DUPIXENT® As Standard of CareDigestive System Diseases, Eosinophilia, Hemic and Lymphatic Diseases, Hypersensitivity, Immediate, digestive system disorder, eosinophilic esophagitis, esophageal disorder, esophagitis, gastroenteritis, hematologic disorder, immune system disorder, leukocyte disorderActive, not recruitingNot stated2026-08-12NCT06693531
Long-term Efficacy, Safety and Tolerability of Iptacopan in C3G or IC-MPGNFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, complement 3 glomerulopathy, glomerulonephritis, immune system disorder, kidney disorder, membranoproliferative glomerulonephritis, nephritis, urinary system disorderRecruitingPhase 32026-08-07NCT03955445
Lead Evaluation for Defibrillation and Reliability Post Approval StudyArrhythmias, Cardiac, Cardiac Conduction System Disease, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Tachyarrhythmia, Tachycardia, cardiovascular disorder, heart disorderEnrolling by invitationNot stated2026-08-03NCT07005232
An Interventional Study of Infigratinib in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 2 / Phase 32026-07-16NCT06873035
Prospective Clinical Assessment Study in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaRecruitingNot stated2026-07-16NCT06410976
Physiologic Response to Bariatric Surgery and the Impact of Adjunct Semaglutide in AdolescentsAdolescent Obesity, Body Weight, Body Weight Changes, Body-Weight Trajectory, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Pediatric Obesity, Signs and Symptoms, Weight Loss Trajectory, nutritional disorder, obesity disorder, overnutritionRecruitingPhase 12026-07-15NCT06575738
Parent Management Training to Treat IrritabilityAnger; Irritable Mood; Temper TantrumRecruitingNot applicable2026-07-15NCT06020261
Study of Efficacy and Safety of Iptacopan in Participants With IC-MPGNFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urination Disorders, Urogenital Diseases, Urological Manifestations, proteinuria, urinary system disorderRecruitingPhase 32026-07-13NCT05755386
Study of Efficacy and Safety of Iptacopan in Patients With C3 Glomerulopathy.Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urination Disorders, Urogenital Diseases, Urological Manifestations, complement 3 glomerulopathy, proteinuria, urinary system disorderRecruitingPhase 32026-07-13NCT04817618
A Study to Evaluate Efficacy and Safety of Perampanel Administered as an Adjunctive Therapy in Pediatric Participants With Childhood EpilepsyNeurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, nervous system disorder, visual epilepsyActive, not recruitingPhase 22026-07-10NCT04015141
Antisense Oligonucleotide Treatment for PCARP Disease Due to Mutation in FLVCR1posterior column ataxia-retinitis pigmentosa syndromeEnrolling by invitationEarly phase 12026-05-19NCT06565572
Development and Evaluation of a Screening Approach for Sexual Dysfunction in AYA Patients With and Surviving Childhood Cancerchildhood malignant neoplasm, neoplasmRecruitingNot applicable2026-05-06NCT05524610
A Trial of Etelcalcetide in Pediatric Participants With Secondary Hyperparathyroidism and Chronic Kidney Disease on HemodialysisChronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, endocrine system disorder, hyperparathyroidism, kidney disorder, kidney failure, parathyroid gland disorder, secondary hyperparathyroidism, urinary system disorderRecruitingPhase 32026-02-27NCT03633708
Preventing Asthma in High Risk KidsHypersensitivity, Immediate, Respiratory Hypersensitivity, asthma, bronchial disorder, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderActive, not recruitingPhase 22025-12-04NCT02570984
Assessment of Endometrial Thickness Among Adolescent and Young Adult Patients on Estrogen Replacement Therapy Using Daily Oral Micronized Progesterone Versus the Etonogestrel Implant.Adnexal Diseases, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Urogenital Diseases, endocrine system disorder, female reproductive system disorder, gonadal disorder, hypogonadism, hypogonadotropic hypogonadism, ovarian disorder, primary ovarian failureRecruitingNot stated2024-12-06NCT06357442