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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess a Medicine Called Tovorafenib in Japanese Children and Young Adults With Brain Tumourslow grade gliomaActive, not recruitingPhase 12026-10-01NCT07441707
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIBCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosisActive, not recruitingPhase 1 / Phase 22026-10-01NCT06488924
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaRecruitingPhase 2 / Phase 32026-09-24NCT07441876
Study to ONO-4538 in Patients With Rhabdoid TumorNeoplasms by Histologic Type, mixed neoplasm, neoplasm, rhabdoid tumorRecruitingPhase 22026-08-04NCT06622941
Safety and Pharmacokinetics Study of Naldemedine in Paediatric Participants Receiving OpioidsChemically-Induced Disorders, Narcotic-Related Disorders, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Digestive, constipation disorder, opioid-induced constipation, psychiatric disorder, substance-related disorderRecruitingPhase 1 / Phase 22026-07-28NCT05588323
Interfant-21 Treatment Protocol for Infants Under 1 Year With KMT2A-rearranged ALL or Mixed Phenotype Acute LeukemiaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute biphenotypic leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, mixed phenotype acute leukemia, neoplasmRecruitingPhase 32026-07-10NCT05327894
Multisite Inventory of Neonatal-Perinatal Interventions (MINI) Minimum DatasetFemale Urogenital Diseases and Pregnancy Complications, Obstetric Labor Complications, Obstetric Labor, Premature, Premature Birth, Urogenital Diseases, pregnancy disorderRecruitingNot stated2026-07-06NCT05685745