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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIBCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosisActive, not recruitingPhase 1 / Phase 22026-10-01NCT06488924

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OrganizationsLinked trials
JCR Pharmaceuticals Co., Ltd.8

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