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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Find Out How EMPAgliflozin is Tolerated and if it Helps Children and Adolescents With Chronic KIDNEY Disease (EMPA-KIDNEY® Kids)Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderRecruitingPhase 32026-09-16NCT07107945
Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia Without InhibitorsHaemophilia A Without Inhibitors; Haemophilia B Without InhibitorsActive, not recruitingPhase 32026-09-16NCT04082429
Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia With InhibitorsHaemophilia A With Inhibitors; Haemophilia B With InhibitorsActive, not recruitingPhase 32026-09-09NCT04083781
Optimising Breathing Support at Extubation in Very Preterm Infants: A Clinical StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Infant, Premature, Diseases, Respiration Disorders, Respiratory Distress Syndrome, Newborn, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderRecruitingNot applicable2026-08-26NCT07251790
Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative ColitisDigestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisActive, not recruitingPhase 32026-08-03NCT04624230
Minimising Adverse Drug Reactions and Verifying Economic Legitimacy in Children (MARVEL-PIC)neoplasmActive, not recruitingNot applicable2026-07-29NCT05667766
Phase 2b Study of RPT904 as Monotherapy in Participants With IgE-Mediated Food AllergyEgg Hypersensitivity, Hypersensitivity, Immediate, Milk Hypersensitivity, Nut and Peanut Hypersensitivity, Peanut Hypersensitivity, food allergy, immune system disorderRecruitingPhase 22026-07-28NCT07220811
A Study of Axatilimab at 3 Different Doses in Participants With Chronic Graft Versus Host Disease (cGVHD)Bronchiolitis Obliterans, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderRecruitingPhase 22026-06-16NCT04710576
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-05-22NCT05881408
A Trial of Targeted Therapies for Patients With Slow-Flow or Fast-Flow Vascular MalformationsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Lymphatic Abnormalities, Neoplasm, Lymphatic Tissue, Neoplasms by Histologic Type, PIK3CA-related overgrowth spectrum, Skin and Connective Tissue Diseases, arteriovenous hemangioma/malformation, cardiovascular disorder, cystic hygroma, lymphangioma, lymphatic malformation, lymphatic system disorder, neoplasm, skin disorder, skin vascular disease, vascular disorder, vascular malformation, venous hemangiomaRecruitingPhase 22026-05-05NCT05983159
Improving Early Intervention in Hearing Impaired Children Using Functional Near-Infrared Spectroscopy (fNIRS)Ear Diseases, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, hearing disorder, hearing loss disorder, nervous system disorder, otorhinolaryngologic diseaseRecruitingNot applicable2025-08-19NCT05847426