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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-05-22NCT05881408

2 results · Page 1 of 1

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OrganizationsLinked trials
Hoffmann-La Roche280
Sarepta Therapeutics, Inc.15

46 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Arkansas Children's HospitalLittle RockUnited States82
Boston Children's HospitalBostonUnited States343
Centre Hospitalier Universitaire de Québec - Université Laval (pavillon Centre Hospitalier Universitaire Laval)QuébecCanada1
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Children's Hospital of The King's DaughtersNorfolkUnited States7
Gangnam Severance Hospital, Yonsei University Health SystemSeoulSouth Korea21
Great Ormond Street Hospital for Children Foundation TrustLondonUnited Kingdom1
Hong Kong Children's HospitalHong KongHong Kong13
Hospital Sant Joan de DeuEsplugues de LlobregatSpain6
Hospital Universitari Politecnic La FeValenciaSpain1
Institute of Neruology, Schneider Children's Medical Center of IsraelPetah TikvaIsrael1
Institute of Translational and Clinical ResearchNewcastle upon TyneUnited Kingdom1
IRCCS Istituto Neurologico Carlo Besta Neurepsichiatria Infantile 2 - Epilettologia e Neurologia dello SviluppoMilanItaly1
Kaohsiung Medical University Chung-Ho Memorial HospitalKaohsiung CityTaiwan48
Karolinska Universitetssjukhuset/Astrid Lindgrens Barnsjukhus, BarnneurologenSolnaSweden1
Kyungpook National University HospitalDaeguSouth Korea44
Lenox Baker Children's Hospital (Duke University)DurhamUnited States2
LMU- Klinikum der Universitat Munchen, Kinderklinik und Kinderpoliklinik im Dr. von Haunerschen Kinderspital, Abeteilung Neuropadiatrie, Campus InnenstadtMünchenGermany1
Lucile Packard Children's Hospital StanfordPalo AltoUnited States20
National Center of Neurology and PsychiatryKodairaJapan12
National Hospital Organization Osaka Toneyama Medical CenterToyonaka-ShiJapan2
National Taiwan University HospitalTaipeiTaiwan203
Nationwide Children's HospitalColumbusUnited States309
Oxford University Hospitals NHS Foundation TrustOxfordUnited Kingdom1