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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Mirikizumab (LY3074828) in Pediatric Participants With Crohn's DiseaseCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderRecruitingPhase 32026-10-07NCT05509777
The AIRTIVITY™ Study: A Study to Find Out Whether BI 1291583 Helps People With Bronchiectasisbronchial disorder, bronchiectasis, respiratory system disorderRecruitingPhase 32026-10-01NCT06872892
A Protocol of Icotrokinra Therapy in Adult and Adolescent Participants With Moderately to Severely Active Ulcerative ColitisDigestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisRecruitingPhase 32026-09-25NCT07196748
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorderActive, not recruitingPhase 32026-06-10NCT05898620
International Registry of Congenital Portosystemic Shunt (IRCPSS)46,XX disorder of sex development, Brain Diseases, Metabolic, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hepatic Insufficiency, Hyperammonemia, Hyperandrogenism, Insulin Resistance, Liver Neoplasms, Male Urogenital Diseases, Neoplasms by Site, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenogenital syndrome, brain disorder, cardiovascular disorder, central nervous system disorder, congenital portosystemic shunt, disorder of sexual differentiation, endocrine system disorder, glucose metabolism disease, gonadal disorder, hepatic encephalopathy, hepatopulmonary syndrome, hyperinsulinism, hypertensive disorder, hypoglycemia, liver disorder, liver failure, lung disorder, metabolic disease, neoplasm, nervous system disorder, pulmonary hypertension, respiratory system disorder, vascular disorder, vascular malformationEnrolling by invitationNot stated2025-06-18NCT06041906