A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Active, not recruiting · NCT05898620 · Registry updated 2026-06-10Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorder | Active, not recruiting | Phase 3 | 2026-06-10 | NCT05898620 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Neurogene Inc. | 2 |
16 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Boston Children's Hospital | Boston | United States | 343 |
| Children's Hospital Colorado | Aurora | United States | 312 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 434 |
| Kennedy Krieger Institute | Baltimore | United States | 41 |
| Manchester University NHS Foundation Trust | Manchester | United Kingdom | 22 |
| Montefiore Medical Center | New York | United States | 21 |
| Nationwide Children's Hospital | Columbus | United States | 309 |
| Nicklaus Children's Hospital Research Institute | Miami | United States | 1 |
| Royal Hospital for Children and Young People | Edinburgh | United Kingdom | 5 |
| Rush University Medical Center | Chicago | United States | 283 |
| Texas Children's Hospital | Houston | United States | 187 |
| The Children's Hospital at Westmead | Sydney | Australia | 4 |
| UCSF Benioff Children's Hospital Oakland | Oakland | United States | 85 |
| UNC at Chapel Hill | Chapel Hill | United States | 1 |
| University of Alabama at Birmingham | Birmingham | United States | 193 |
| Vanderbilt University Medical Center | Nashville | United States | 427 |