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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingPhase 22026-10-08NCT07287982
A Research Study on How Well Concizumab Works for You if You Have Haemophilia A or B With or Without InhibitorsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingPhase 32026-09-18NCT05135559
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 32026-09-17NCT06612268
I-DECIDE After Bronchiolitis HospitalizationBronchiolitis AcuteRecruitingNot applicable2026-09-10NCT07243652
TINI 2: Total Therapy for Infants With Acute Lymphoblastic Leukemia IIHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 1 / Phase 22026-06-03NCT05848687
STEP TEENS Weight Maintenance: A Research Study on How Well Semaglutide Helps Teenagers With Excess Body Weight to Lose Weight and Maintain Weight LossBody Weight, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, nutritional disorder, obesity disorder, overnutritionActive, not recruitingPhase 42026-06-02NCT06571383
Implementation of the Pain and Irritability of Unknown Origin (PIUO) Pathway in Community Pediatric PracticesNeurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, nervous system disorder, neuralgia, neuromuscular disease, peripheral nervous system disorderRecruitingNot applicable2025-03-11NCT06869928
Management of Type 1 Supracondylar Humeral FracturesArm Injuries, Elbow Fractures, Elbow Injuries, bone fracture, injuryRecruitingNot applicable2024-12-11NCT04642807
Simple Bone Cysts in KidsCysts, bone disorder, musculoskeletal system disorder, neoplasm, solitary bone cystRecruitingPhase 32023-07-12NCT02193841