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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingPhase 22026-10-08NCT07287982

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OrganizationsLinked trials
argenx52

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Research sitesCityCountryLinked trials
Addenbrooke's HospitalCambridgeUnited Kingdom14
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Arkansas Children's HospitalLittle RockUnited States82
BC Children's HospitalVancouverCanada9
Birmingham Heartlands HospitalBirminghamUnited Kingdom3
Boston Children's HospitalBostonUnited States343
Children's Hospital Philadelphia - NeurologyPhiladelphiaUnited States1
Childrens Hospital of The Kings DaughtersNorfolkUnited States1
Columbia University Herbert Irving Comprehensive Cancer CenterNew YorkUnited States7
Connecticut Children's Medical CenterHartfordUnited States106
Great Ormond Street Hospital for ChildrenLondonUnited Kingdom1
Leeds General InfirmaryLeedsUnited Kingdom4
MDUK Oxford Neuromuscular CentreOxfordUnited Kingdom1
Neurology Rare Disease CenterFlower MoundUnited States8
Rady Childrens HospitalSan DiegoUnited States2
Rare Disease Research FL LLCKissimmeeUnited States1
Rare Disease Research NC, LLCHillsboroughUnited States1
Royal Children's HospitalParkvilleAustralia40
Royal Hospital for ChildrenGlasgowUnited Kingdom1
Sheffield Children's HospitalSheffieldUnited Kingdom4
Stanford University Medical CenterStanfordUnited States43
Sydney Children's Hospital, RandwickRandwickAustralia2
Texas Children's HospitalHoustonUnited States187
The Curators of the University of Missouri on behalf of University of Missouri Health CareColumbiaUnited States2
The Hospital For Sick ChildrenTorontoCanada94