IRCCS Ospedale Pediatrico Bambino Gesù
IRCCS Ospedale Pediatrico Bambino Gesù
Roma, Italy2 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| An Open-label, Phase 2 Pilot Study on the Efficacy and Safety of Piclidenoson in Patients With Lowe Syndrome | Abnormalities, Multiple, Amino Acid Transport Disorders, Inborn, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Diseases, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, kidney disorder, metabolic disease, nervous system disorder, oculocerebrorenal syndrome, renal tubular transport disease, urinary system disorder | Not yet recruiting | Phase 2 | 2026-02-18 | NCT07410455 | |
| CD19-CAR_Lenti T Cells in Pediatric Patients Affected by Relapsed/Refractory CD19+ ALL and DLBCL or PML | B-cell neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, diffuse large B-cell lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, mediastinal malignant lymphoma, neoplasm | Active, not recruiting | Phase 1 / Phase 2 | 2025-12-02 | NCT04787263 |