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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Open-label, Phase 2 Pilot Study on the Efficacy and Safety of Piclidenoson in Patients With Lowe SyndromeAbnormalities, Multiple, Amino Acid Transport Disorders, Inborn, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Diseases, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, kidney disorder, metabolic disease, nervous system disorder, oculocerebrorenal syndrome, renal tubular transport disease, urinary system disorderNot yet recruitingPhase 22026-02-18NCT07410455

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OrganizationsLinked trials
Can-Fite BioPharma4

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Research sitesCityCountryLinked trials
IRCCS Ospedale Pediatrico Bambino GesùRomaItaly2