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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia BCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 1 / Phase 22026-10-08NCT06379789
Von Willebrand Factor in Pregnancy (VIP) StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Hemorrhage, Obstetric Labor Complications, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postpartum Hemorrhage, Urogenital Diseases, Uterine Hemorrhage, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, pregnancy disorder, puerperal disorder, von Willebrand disease (hereditary or acquired)RecruitingNot stated2025-12-18NCT04146376