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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Targeted Immunotherapy After Myeloablative TBI-Based Conditioning & AlloHCT in CAYA With High Risk T-Cell ALL & LymphomaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Precursor T-Cell Lymphoblastic Leukemia-Lymphoma, T-cell acute lymphoblastic leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 12026-09-11NCT04972942
Treatment of Refractory BK Infections With Related Donor BK Specific Cytotoxic T-cells (CTLs)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infections, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunity, viral infectious diseaseRecruitingPhase 1 / Phase 22026-04-15NCT04197596
SARS-CoV-2 CTLS for Mild to Moderate COVID-19 DiseaseCOVID-19, Coronaviridae Infections, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease, viral pneumoniaRecruitingPhase 1 / Phase 22026-04-13NCT04896606
CMV CTLs in Neonates With CMV InfectionPathologic Processes, Pathological Conditions, Signs and Symptoms, diseaseRecruitingPhase 22026-03-30NCT05564598
Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene TransferCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, juvenile neuronal ceroid lipofuscinosis, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseActive, not recruitingNot stated2025-10-02NCT04273243
EBV-specific Cytotoxic T-lymphocytes (CTLs) for Refractory EBV InfectionCongenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Virus Infections, Epstein-Barr virus infection, Herpesviridae infectious disease, Infections, Primary Immunodeficiency Diseases, Tumor Virus Infections, hereditary disease, immune system disorder, inborn error of immunity, viral infectious diseaseRecruitingPhase 22025-08-08NCT03266653
Virus Specific Cytotoxic T-Lymphocytes (CTLs) for Refractory Cytomegalovirus (CMV)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Virus Infections, Herpesviridae infectious disease, Infections, Primary Immunodeficiency Diseases, cytomegalovirus infection, hereditary disease, immune system disorder, inborn error of immunity, viral infectious diseaseRecruitingPhase 22025-08-08NCT03266640
Adenovirus-specific Cytotoxic T-lymphocytes for Refractory Adenovirus InfectionCongenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Virus Infections, Infections, Primary Immunodeficiency Diseases, adenoviridae infectious disease, hereditary disease, immune system disorder, inborn error of immunity, viral infectious diseaseRecruitingPhase 22025-08-08NCT03266627
Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMDBecker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingNot stated2024-08-27NCT02972580