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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene TransferCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, juvenile neuronal ceroid lipofuscinosis, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseActive, not recruitingNot stated2025-10-02NCT04273243

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OrganizationsLinked trials
Emily de los Reyes3

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Research sitesCityCountryLinked trials
Nationwide Children's HosptialColumbusUnited States9