Weill Cornell Medicine; Division of Pediatric Neurology

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)	Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Canavan disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease	Recruiting	Phase 1 / Phase 2	2026-04-17		NCT04998396

Clinical trials