A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
Recruiting · NCT04998396 · Registry updated 2026-04-17Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Canavan disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease | Recruiting | Phase 1 / Phase 2 | 2026-04-17 | NCT04998396 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Aspa Therapeutics | 1 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 144 |
| Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND) | Boston | United States | 1 |
| UCSF Benioff Children's Hospital Oakland | Oakland | United States | 85 |
| Weill Cornell Medicine; Division of Pediatric Neurology | New York | United States | 1 |