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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated CardiomyopathyCardiomegaly, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, aortic valve disorder, aortic valve stenosis, cardiomyopathy, cardiovascular disorder, dilated cardiomyopathy, heart disorder, heart valve disorder, hereditary disease, hypertrophic cardiomyopathy, laminopathy, restrictive cardiomyopathy, subvalvular aortic stenosisActive, not recruitingNot stated2026-09-02NCT05112237
Non-invasive Prediction of EArly Cardiac rEjectionCardiac MRI; Cell Free DNA; Heart Transplant; Pediatric Heart Transplant; RejectionRecruitingNot stated2026-08-20NCT07770659
Xeltis Bioabsorbable Pulmonary Valved Conduit Pivotal StudyCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderActive, not recruitingNot applicable2026-08-06NCT03022708
Mobile Video Directly Observed Therapy (DOT) for Immunosuppression Medication Adherence in Adolescent Heart Transplant RecipientsHealth Behavior; Heart Transplant Rejection; Immune Suppression; Medication Nonadherence; Patient Engagement; Pediatric Heart Transplant; Remote MonitoringRecruitingNot applicable2026-07-16NCT05732779
Standardizing Treatments for Pulmonary Exacerbations - Aminoglycoside StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 42026-07-08NCT05548283
Multisite Inventory of Neonatal-Perinatal Interventions (MINI) Minimum DatasetFemale Urogenital Diseases and Pregnancy Complications, Obstetric Labor Complications, Obstetric Labor, Premature, Premature Birth, Urogenital Diseases, pregnancy disorderRecruitingNot stated2026-07-06NCT05685745
The Diaphragmatic Initiated Ventilatory Assist (DIVA) TrialCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Death, Infant, Newborn, Diseases, Infant, Premature, Diseases, Lung Injury, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Ventilator-Induced Lung Injury, bronchopulmonary dysplasia, lung disorder, respiratory system disorderRecruitingNot applicable2026-06-25NCT05446272
Safety, Tolerability and Efficacy Study of ARCT-032 in People With Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 22026-05-08NCT06747858
Long-Term Outcomes After the Multisystem Inflammatory Syndrome in Childrenpediatric multisystem inflammatory disease, COVID-19 relatedActive, not recruitingNot stated2026-03-27NCT05287412
Comparison of Methods of Pulmonary Blood Flow Augmentation in Neonates: Shunt Versus Stent (The COMPASS Trial)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderActive, not recruitingNot applicable2026-01-07NCT05268094
Allied Cleft & Craniofacial Quality-Improvement and Research Network (ACCQUIREnet)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Jaw Abnormalities, Jaw Diseases, Maxillofacial Abnormalities, Mouth Abnormalities, Musculoskeletal Abnormalities, Stomatognathic Diseases, Stomatognathic System Abnormalities, cleft lip, cleft lip/palate, cleft palate, lip disorder, mouth disorder, musculoskeletal system disorderEnrolling by invitationNot stated2026-01-07NCT02702869
Prospective Study of Pregnancy in Women With Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingNot stated2025-11-03NCT04828382
Fontan Udenafil Exercise Longitudinal Assessment Trial - 2Single Ventricle Heart DiseaseRecruitingPhase 32025-10-28NCT05918211
Percutaneous Intervention Versus Observational Trial of Arterial Ductus in Low Weight InfantsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, patent ductus arteriosusRecruitingNot applicable2025-03-30NCT05547165