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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated CardiomyopathyCardiomegaly, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, aortic valve disorder, aortic valve stenosis, cardiomyopathy, cardiovascular disorder, dilated cardiomyopathy, heart disorder, heart valve disorder, hereditary disease, hypertrophic cardiomyopathy, laminopathy, restrictive cardiomyopathy, subvalvular aortic stenosisActive, not recruitingNot stated2026-09-02NCT05112237

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OrganizationsLinked trials
Tenaya Therapeutics4

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Research sitesCityCountryLinked trials
Arkansas Children's HospitalLittle RockUnited States82
Cardiology Care for ChildrenLancasterUnited States1
Children's Hospital Los AngelesLos AngelesUnited States226
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Children's Medical Center DallasDallasUnited States2
Children's Mercy Hospital KansasKansas CityUnited States1
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Cleveland Clinic Main CampusClevelandUnited States30
Cohen Children's Medical CenterLake SuccessUnited States2
Columbia University Irving Medical CenterNew YorkUnited States234
DDC Clinic Center for Special Needs ChildrenMiddlefieldUnited States1
Great Ormond Street Hospital For Children Nhs Foundation TrustLondonUnited Kingdom23
Hospital Alvaro Cunqueiro - Clinico Universitario VigoVigoSpain1
Hospital General Universitario Gregorio MarañónMadridSpain1
Hospital Sant Joan de Déu BarcelonaBarcelonaSpain1
Joe DiMaggio Children's HospitalHollywoodUnited States14
Montefiore Medical Center, Albert Einstein College of MedicineThe BronxUnited States2
Mount SinaiNew YorkUnited States58
Nemours Alfred I. Dupont Hospital for ChildrenWilmingtonUnited States5
NHS Greater Glasgow and ClydeGlasgowUnited Kingdom4
Rady Children's Hospital - San DiegoSan DiegoUnited States65
Royal Brompton & Harefield NHS Foundation TrustLondonUnited Kingdom4
St. Louis Children's HospitalSt LouisUnited States30
Texas Children's HospitalHoustonUnited States187
The Hospital for Sick ChildrenTorontoCanada20