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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisiseye disorder, retinal degeneration, retinal disorder, retinoschisisRecruitingPhase 32026-09-29NCT05878860
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 1 / Phase 22026-07-08NCT06138639
TRIAGE-GS: Towards Reducing Inefficiencies Affecting Genetics Encounters Through Genome SequencingGenetic ConditionsEnrolling by invitationNot applicable2026-04-24NCT06935019
Optimizing Nutrition and Milk (Opti-NuM) ProjectEarly Nutrition and the Preterm Infant; Growth &Amp; Development; Human Milk Feeding; Human Milk Fortification; Human Milk Microbiome; Human Milk Nutrition; Nutritional Requirements; Very Low Birth Weight BabyRecruitingNot stated2025-03-11NCT06870981