A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Recruiting · NCT06138639 · Registry updated 2026-07-08Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Phase 1 / Phase 2 | 2026-07-08 | NCT06138639 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Solid Biosciences Inc. | 5 |
15 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 4 |
| Arkansas Children's Hospital | Little Rock | United States | 82 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 434 |
| Children's Hospital of The King's Daughters | Norfolk | United States | 7 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | Rome | Italy | 34 |
| Great Ormond Street Hospital | London | United Kingdom | 38 |
| Nationwide Children's Hospital | Columbus | United States | 12 |
| Oregon Health and Sciences University | Portland | United States | 20 |
| Rare Disease Research | Atlanta | United States | 12 |
| Seattle Children's Hospital | Seattle | United States | 281 |
| The Hospital for Sick Children | Toronto | Canada | 4 |
| University of California | San Diego | United States | 2 |
| University of California, Davis | Sacramento | United States | 49 |
| University of California, Los Angeles Medical Center | Los Angeles | United States | 3 |
| Washington University in St. Louis | St Louis | United States | 79 |