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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Fabry Disease Registry & Pregnancy Sub-registryBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, X-linked disease, angiokeratoma, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, neoplasm, nervous system disorder, sphingolipidosis, vascular cancer, vascular disorderRecruitingNot stated2026-06-23NCT00196742

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OrganizationsLinked trials
Genzyme, a Sanofi Company22

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840013ChicagoUnited States3
Arkansas Children's Hospital- Site Number : 840109Little RockUnited States3
Atlantic Health System- Site Number : 840099MorristownUnited States3
Atrium Health - Carolinas Medical Center- Site Number : 840065CharlotteUnited States1
Baylor Institute of Metabolic Disease- Site Number : 840058DallasUnited States3
Baystate Medical Center- Site Number : 840002SpringfieldUnited States2
Boston Children's Hospital- Site Number : 840092BostonUnited States2
Brigham & Women's Hospital- Site Number : 840103BostonUnited States1
Centro de Pesq Materno Infantil de Campinas- Site Number : 076009CampinasBrazil1
Centro Saude Escola Joel Domingos Machado- Site Number : 076002Ribeirão PretoBrazil1
Children's Hospital of Michigan- Site Number : 840066DetroitUnited States3
Children's Hospital of Orange County- Site Number : 840074OrangeUnited States3
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089PhiladelphiaUnited States3
Children's Hospital of Philadelphia- Site Number : 840034PhiladelphiaUnited States3
Children's Hospital of The King's Daughters- Site Number : 840072NorfolkUnited States3
Children's Hospitals and Clinics of Minnesota- Site Number : 840046MinneapolisUnited States3
Children's Hospitals and Clinics of Minnesota- Site Number : 840114MinneapolisUnited States3
Children's National Medical Center - Washington- Site Number : 840067Washington D.C.United States3
Children's Specialty Center - Las Vegas- Site Number : 840008Las VegasUnited States3
Children's Wisconsin- Site Number : 840054MilwaukeeUnited States2
Cincinnati Children's Hospital Medical Center (Cincinnati Children's Hospital)- Site Number : 840033CincinnatiUnited States1
Cleveland Clinic - Cleveland- Site Number : 840048ClevelandUnited States3
Clínica Senhor do Bonfim- Site Number : 076008Feira de SantanaBrazil1
Cook Children's Medical Center- Site Number : 840024Fort WorthUnited States2
Cooper Health Center- Site Number : 840098CamdenUnited States1