Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pompe Disease Registry ProtocolBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderRecruitingNot stated2026-06-23NCT00231400

1 results · Page 1 of 1

Swipe the table sideways for more columns.

OrganizationsLinked trials
Genzyme, a Sanofi Company22

101 results · Page 1 of 5

Swipe the table sideways for more columns.

Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840011ChicagoUnited States2
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840013ChicagoUnited States3
Arkansas Children's Hospital- Site Number : 840109Little RockUnited States3
Atlantic Health System- Site Number : 840099MorristownUnited States3
Barrow Neurological Institute- Site Number : 840087PhoenixUnited States1
Baylor Institute of Metabolic Disease- Site Number : 840058DallasUnited States3
Baystate Medical Center- Site Number : 840002SpringfieldUnited States2
Boston Children's Hospital- Site Number : 840092BostonUnited States2
Carolinas Medical Center Hospital- Site Number : 840065CharlotteUnited States2
Children's Hospital Colorado - Aurora- Site Number : 840069AuroraUnited States1
Children's Hospital of Michigan- Site Number : 840066DetroitUnited States3
Children's Hospital of Orange County- Site Number : 840074OrangeUnited States3
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089PhiladelphiaUnited States3
Children's Hospital of Philadelphia- Site Number : 840034PhiladelphiaUnited States3
Children's Hospital of The King's Daughters- Site Number : 840072NorfolkUnited States3
Children's Hospitals and Clinics of Minnesota- Site Number : 840046MinneapolisUnited States3
Children's Hospitals and Clinics of Minnesota- Site Number : 840114MinneapolisUnited States3
Children's Mercy Adelle Hall Campus- Site Number : 840063Kansas CityUnited States2
Children's National Medical Center - Washington- Site Number : 840067Washington D.C.United States3
Children's Specialty Center - Las Vegas- Site Number : 840008Las VegasUnited States3
Children's Wisconsin- Site Number : 840054MilwaukeeUnited States2
Cleveland Clinic - Cleveland- Site Number : 840048ClevelandUnited States3
Columbia University Irving Medical Center- Site Number : 840125New YorkUnited States2
Cook Children's Medical Center- Site Number : 840024Fort WorthUnited States2
Cooper Health Center- Site Number : 840098CamdenUnited States2