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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registryBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisRecruitingNot stated2026-04-14NCT00358943

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OrganizationsLinked trials
Genzyme, a Sanofi Company22

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840011ChicagoUnited States2
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840013ChicagoUnited States3
Arkansas Children's Hospital- Site Number : 840109Little RockUnited States3
Atlantic Health System- Site Number : 840099MorristownUnited States3
Baylor Institute of Metabolic Disease- Site Number : 840058DallasUnited States3
Boston Children's Hospital - PIN- Site Number : 840092BostonUnited States1
Carolinas Medical Center Hospital- Site Number : 840065CharlotteUnited States2
Children's Hospital of Michigan- Site Number : 840066DetroitUnited States3
Children's Hospital of Orange County- Site Number : 840074OrangeUnited States3
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089PhiladelphiaUnited States3
Children's Hospital of Philadelphia- Site Number : 840034PhiladelphiaUnited States3
Children's Hospital of The King's Daughters- Site Number : 840072NorfolkUnited States3
Children's Hospital of Wisconsin-Pediatrics- Site Number : 840054MilwaukeeUnited States1
Children's Hospitals and Clinics of Minnesota- Site Number : 840046MinneapolisUnited States3
Children's Hospitals and Clinics of Minnesota- Site Number : 840114MinneapolisUnited States3
Children's Mercy Adelle Hall Campus- Site Number : 840063Kansas CityUnited States2
Children's National Medical Center - Washington- Site Number : 840067Washington D.C.United States3
Children's Specialty Center - Las Vegas- Site Number : 840008Las VegasUnited States3
Cincinnati Children's Hospital Medical Center- Site Number : 840026CincinnatiUnited States1
Cleveland Clinic - Cleveland- Site Number : 840048ClevelandUnited States3
Columbia University Irving Medical Center- Site Number : 840125New YorkUnited States2
Cook Children's Health Care System- Site Number : 840024Fort WorthUnited States1
Cooper Health Center- Site Number : 840098CamdenUnited States2
Duke University Medical Center Genetics Dept- Site Number : 840037DurhamUnited States3
Emory University School of Medicine- Human Genetics- Site Number : 840060DecaturUnited States3