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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderRecruitingNot stated2026-04-08NCT01665326

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OrganizationsLinked trials
Duke University446
Genzyme, a Sanofi Company22

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Research sitesCityCountryLinked trials
Duke University Medical CenterDurhamUnited States505