Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:
Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:
Active, not recruiting · NCT02616484 · Registry updated 2025-05-04Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pyruvate Dehydrogenase Complex Deficiency Disease, Pyruvate Metabolism, Inborn Errors, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorder | Active, not recruiting | Phase 3 | 2025-05-04 | NCT02616484 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Medosome Biotec LLC | 1 |
| Saol Therapeutics Inc | 2 |
10 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Baylor College of Medicine | Houston | United States | 306 |
| Children'S Hospital of Orange County | Orange | United States | 128 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 2 |
| Children's Hospital of Pittsburgh | Pittsburgh | United States | 16 |
| Children's National Medical Center | Washington D.C. | United States | 177 |
| Seattle Children's Hospital | Seattle | United States | 281 |
| Stanford University | Stanford | United States | 213 |
| University Hospitals Cleveland Medical Center | Cleveland | United States | 234 |
| University of Florida | Gainesville | United States | 79 |
| University of Utah | Salt Lake City | United States | 16 |