A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
Active, not recruiting · NCT03019406 · Registry updated 2026-01-30Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa | Glycogen Storage Disease Type II-Pompe's Disease | Active, not recruiting | Phase 2 | 2026-01-30 | NCT03019406 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Genzyme, a Sanofi Company | 22 |
3 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Duke University Medical Center Site Number : 8400001 | Durham | United States | 1 |
| Regional Medical Genetics Center of New York Site Number : 8400002 | Valhalla | United States | 1 |
| Seattle Childrens Hospital and Regional Medical Center- Site Number : 8400005 | Seattle | United States | 1 |