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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gaucherite - A Study to Stratify Gaucher DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher Disease, Type 1, Gaucher Disease, Type 3, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisRecruitingNot stated2024-08-06NCT03240653

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Research sitesCityCountryLinked trials
Birmingham Childrens HospitalBirminghamUnited Kingdom1
Cambridge University HospitalCambridgeUnited Kingdom4
Great Ormond Street HospitalLondonUnited Kingdom15
National Hospital for Neurology and NeurosurgeryLondonUnited Kingdom4
New Queen Elizabeth HospitalBirminghamUnited Kingdom1
Royal Free HospitalLondonUnited Kingdom24
Royal Manchester Childrens HospitalManchesterUnited Kingdom3
Salford Royal NHS Foundation TrustSalfordUnited Kingdom4