Autologous Gene Therapy for Artemis-Deficient SCID
Autologous Gene Therapy for Artemis-Deficient SCID
Recruiting · NCT03538899 · Registry updated 2026-02-13Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Autologous Gene Therapy for Artemis-Deficient SCID | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunity, metabolic disease, severe combined immunodeficiency | Recruiting | Phase 1 / Phase 2 | 2026-02-13 | NCT03538899 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| University of California, San Francisco | 637 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| University of California, San Francisco (UCSF) Children's Hospital | San Francisco | United States | 1 |