Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency
Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency
Active, not recruiting · NCT03636438 · Registry updated 2026-06-01Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, ornithine carbamoyltransferase deficiency, urea cycle disorder | Active, not recruiting | Not stated | 2026-06-01 | NCT03636438 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Ultragenyx Pharmaceutical Inc | 24 |
9 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Boston Children's Hospital | Boston | United States | 343 |
| Hopital Femme Mere Enfant | Bron | France | 1 |
| Hospital Clinico Universitario de Santiago | Santiago de Compostela | Spain | 1 |
| Hospital Universitario de Cruces. Servicio de Pediatria | Barakaldo | Spain | 1 |
| Icahn School of Medicine | New York | United States | 2 |
| M.A.G.I.C. Clinic | Calgary | Canada | 1 |
| Queen Elizabeth Hospital, Department of Endocrinology | Birmingham | United Kingdom | 1 |
| The Children's Hospital Colorado | Aurora | United States | 2 |
| University Hospital Cleveland Medical Center/Case Western Reserve University | Cleveland | United States | 1 |