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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis IICongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, X-linked disease, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 2, nervous system disorderActive, not recruitingPhase 22026-09-08NCT03708965

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OrganizationsLinked trials
JCR Pharmaceuticals Co., Ltd.8

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Research sitesCityCountryLinked trials
Grupo de Pesquisa Clínica em Genética Médica - HCPAPorto AlegreBrazil1
Igeim - UnifespSão PauloBrazil1