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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Direct Lentiviral Injection Gene Therapy for MLDBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, Sulfatidosis, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, metachromatic leukodystrophy, nervous system disorder, sphingolipidosisNot yet recruitingNot applicable2026-09-01NCT03725670

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OrganizationsLinked trials
Shenzhen Geno-Immune Medical Institute43

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Research sitesCityCountryLinked trials
Lung-Ji ChangShenzhenChina1