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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderActive, not recruitingPhase 32026-08-31NCT03737214

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OrganizationsLinked trials
Idorsia Pharmaceuticals Ltd.11

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Research sitesCityCountryLinked trials
Baylore University Medical CenterDallasUnited States1
Children's Hospital Research Institute of ManitobaWinnipegCanada1
Clinic of Immunological Diseases and Blood Coagulability Cracow University HospitalKrakowPoland1
Greenwood Genetics CenterGreenvilleUnited States1
Haukeland University HospitalBergenNorway41
Hospital Academisch Medisch Centrum - Department of Internal Medicine, Div. Endrocrinology and MetabolismAmsterdamNetherlands1
Hospital Quironsalud ZaragozaZaragozaSpain1
Hospital Universitari de Bellvitge / Nephrology DptBarcelonaSpain1
Hospital Universitario Ramon y Cajal. Servicio de Medicina InternaMadridSpain1
Infusion AssociatesGrand RapidsUnited States3
London Health Sciences CTR, Victoria HospitalLondonCanada1
Lysosomal and Rare Disorders Research and Treatment Center, Inc.FairfaxUnited States6
Massachusetts General HospitalBostonUnited States1015
Medizinische Universität Wien, Universitätsklinik für Innere Medizin III, Klinische Abteilung für Nephrologie und DialyseViennaAustria1
Narodowy Instytut Kardiologii Stefana kardynała Wyszyńskiego - Państwowy Instytut BadawczyWarsawPoland1
National Hospital For Neurology and NeurosurgeryLondonUnited Kingdom4
Nephrologicum Markgräflerland MVZ GmbHMüllheimGermany1
Psychiatrische Universitätsklinik ZürichZurichSwitzerland2
Raymond Poincaré Hosp - Med Genetics DeptGarchesFrance1
Renal Disease Research Institute LLCDallasUnited States1
Research Center, Hôpital du Sacré-Coeur de MontréalMontrealCanada1
Royal Free London NHS Foundation Trust Lysosomal Storage Disorder Unit; Department of HematologyLondonUnited Kingdom1
Royal Melbourne Hospital - Department of NephrologyParkvilleAustralia1
Royal Perth Hospital, Department of NephrologyPerthAustralia1
Rush University Medical Center - Dept of PediatricsChicagoUnited States1