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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy for Children With CLN3 Batten DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, juvenile neuronal ceroid lipofuscinosis, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseActive, not recruitingPhase 1 / Phase 22026-06-10NCT03770572

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OrganizationsLinked trials
Neela Therapeutics1

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Research sitesCityCountryLinked trials
Nationwide Children's HospitalColumbusUnited States1