A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
Active, not recruiting · NCT03779334 · Registry updated 2026-10-08Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Active, not recruiting | Phase 2 | 2026-10-08 | NCT03779334 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Hoffmann-La Roche | 280 |
7 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Chr de La Citadelle | Liège | Belgium | 16 |
| Hospital das Clinicas - FMUSP_X | São Paulo | Brazil | 2 |
| Kaohsiung Medical University Chung-Ho Hospital | Kaohsiung City | Taiwan | 1 |
| Nemours Children's Hospital | Orlando | United States | 1 |
| Russian Children Neuromuscular Center of Veltischev | Moscow | Russia | 1 |
| Sydney Children's Hospital | Randwick | Australia | 43 |
| Szpital Gdanskiego Uniwersytetu Medycznego | Gda?sk | Poland | 1 |