A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome
A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome
Active, not recruiting · NCT03837483 · Registry updated 2025-09-29Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Primary Immunodeficiency Diseases, Wiskott-Aldrich syndrome, X-linked disease, blood coagulation disease, hematologic disorder, hemorrhagic disease, hereditary disease, immune system disorder, inborn error of immunity, inherited blood coagulation disorder, leukocyte disorder, leukopenia, lymphopenia | Active, not recruiting | Phase 3 | 2025-09-29 | NCT03837483 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Fondazione Telethon | 8 |
| Ospedale San Raffaele | 19 |
2 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Children's Healthcare of Atlanta, Inc | Atlanta | United States | 1 |
| Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) | Milan | Italy | 2 |