A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
Active, not recruiting · NCT03913143 · Registry updated 2022-03-17Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Abnormalities, Eye Diseases, Hereditary, Leber congenital amaurosis, Leber congenital amaurosis 10, Leber hereditary optic neuropathy, Meckel syndrome, type 4, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, blindness (disorder), cranial nerve neuropathy, eye disorder, hereditary disease, hereditary optic atrophy, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, retinal disorder, vision disorder | Active, not recruiting | Phase 2 / Phase 3 | 2022-03-17 | NCT03913143 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| ProQR Therapeutics | 2 |
14 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Amsterdam University Medica Center - Locatie AMC | Amsterdam | Netherlands | 1 |
| Centre de maladies rares CHNO des Quinze Vingt | Paris | France | 3 |
| Eye Clinic University of Campania Luigi Vanvitelli | Naples | Italy | 1 |
| Federal University of São Paulo - Hospital São Paulo (UNIFESP-HSP) | São Paulo | Brazil | 2 |
| Het Oogziekenhuis Rotterdam | Rotterdam | Netherlands | 2 |
| Hospital Civil de Strasbourg | Strasbourg | France | 1 |
| INRET Clínica/ Santa Casa de Misericórdia de Belo Horizonte | Belo Horizonte | Brazil | 2 |
| Justus-Liebig Universität - Department of Ophthalmology | Giessen | Germany | 2 |
| McGill University Health Centre - Centre for Innovative Medicine | Montreal | Canada | 2 |
| Moorfields Eye Hospital - NHS Foundation Trust | London | United Kingdom | 1 |
| The Hospital for Sick Children - SickKids | Toronto | Canada | 2 |
| Universitair Ziekenhuis Gent (UZ) | Ghent | Belgium | 1 |
| University of Iowa | Iowa City | United States | 284 |
| University of Tuebingen - Inst. for Ophthalmic Research | Tübingen | Germany | 2 |