A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal Disease
A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal Disease
Active, not recruiting · NCT04020055 · Registry updated 2026-07-06Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Fabry disease, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, chronic renal failure syndrome, hereditary disease, inborn errors of metabolism, kidney disorder, kidney failure, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, urinary system disorder, vascular disorder | Active, not recruiting | Phase 3 | 2026-07-06 | NCT04020055 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Amicus Therapeutics | 7 |
12 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Centro Hospitalar e Universitário de Coimbra (CHUC) | Coimbra | Portugal | 1 |
| Emory University | Atlanta | United States | 262 |
| Hospital General Universitario de Elda | Elda | Spain | 1 |
| Hospital General Universitario Gregorio Marañon | Madrid | Spain | 72 |
| Hospital Universitari(o) de Bellvitge (HUB) Feixa Llarga | Barcelona | Spain | 1 |
| Lysosomal and Rare Disorders Research and Treatment Center, Inc | Fairfax | United States | 1 |
| Osaka University Hospital | Suita | Japan | 13 |
| Royal Melbourne Hospital | Parkville | Australia | 39 |
| Royal Perth Hospital | Perth | Australia | 2 |
| Salford Royal Hospital | Salford | United Kingdom | 3 |
| Shizuoka General Hospital | Shizuoka | Japan | 2 |
| The Cleveland Clinic | Cleveland | United States | 26 |