A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
Active, not recruiting · NCT04093349 · Registry updated 2024-11-27Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Active, not recruiting | Phase 1 / Phase 2 | 2024-11-27 | NCT04093349 |
1 results · Page 1 of 1
Organizations
Swipe the table sideways for more columns.
| Organizations | Linked trials |
|---|---|
| Spark Therapeutics, Inc. | 4 |
29 results · Page 1 of 2
Research sites
Swipe the table sideways for more columns.