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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderActive, not recruitingPhase 1 / Phase 22024-11-27NCT04093349

1 results · Page 1 of 1

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OrganizationsLinked trials
Spark Therapeutics, Inc.4

29 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Assistance Publique Hôpitaux de MarseilleMarseilleFrance1
Azienda Ospedaliera Universitaria Città della Salute e della Scienza di Torino - Neurology, Osp. MolinetteTorinoItaly1
Barrow Neurological InstitutePhoenixUnited States50
Centre Hospitalier Régional Universitaire de LilleLilleFrance5
Centre Hospitalier Universitaire d'AngersAngersFrance15
CHU Paris IdF Ouest - Hôpital Raymond PoincaréGarchesFrance1
Emory University School of MedicineAtlantaUnited States6
Erasmus Medical CenterRotterdamNetherlands3
Friedrich-Baur-Institut Neurologische Klinik Ludwig-Maximilians-Universität MünchenMünchenGermany1
Lysosomal and Rare Disorders Research & Treatment CenterFairfaxUnited States1
Malattie Metaboliche Universita Degli Studi Di Napoli Federico IINaplesItaly1
Montreal Neurological HospitalMontrealCanada1
New Queen Elizabeth Hospital BirminghamBirminghamUnited Kingdom1
Nice University HospitalNiceFrance1
Oregon Health & Science UniversityPortlandUnited States261
RigshospitaletCopenhagenDenmark1
Salford Royal MHS Foundation TrustSalfordUnited Kingdom1
The Ottawa HospitalOttawaCanada15
The Royal Free London NHS Foundation TrustLondonUnited Kingdom1
Universita Degli Studi Di Messina - Dipartimento di Medicina Clinica e SperimentaleMessinaItaly1
Universita Degli Studi Di Milano, Laboratorio di Biochimica e Genetica della Malattie NeuromuscolariMilanItaly1
University of California Irvine HealthOrangeUnited States4
University of Kansas Medical Center Research InstituteKansas CityUnited States11
University of MinnesotaMinneapolisUnited States325
University of PennsylvaniaPhiladelphiaUnited States507