Gene Transfer Study in Patients With Late Onset Pompe Disease
Gene Transfer Study in Patients With Late Onset Pompe Disease
Active, not recruiting · NCT04174105 · Registry updated 2026-09-02Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Transfer Study in Patients With Late Onset Pompe Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Active, not recruiting | Phase 1 / Phase 2 | 2026-09-02 | NCT04174105 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Astellas Gene Therapies | 6 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Newcastle Upon Tyne Hospitals Foundation Trust Clinical Research Facility | Newcastle upon Tyne | United Kingdom | 1 |
| Stanford University | Palo Alto | United States | 161 |
| University of California Irvine, Department of Neurology | Orange | United States | 1 |
| University of Utah, Division of Medical Genetics | Salt Lake City | United States | 1 |