OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
Active, not recruiting · NCT04283227 · Registry updated 2025-09-05Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, Sulfatidosis, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, metachromatic leukodystrophy, nervous system disorder, sphingolipidosis | Active, not recruiting | Phase 3 | 2025-09-05 | NCT04283227 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Orchard Therapeutics | 5 |
| Ospedale San Raffaele | 19 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) | Milan | Italy | 2 |