Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA
Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA
Enrolling by invitation · NCT04360265 · Registry updated 2026-07-17Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3A | Enrolling by invitation | Phase 3 | 2026-07-17 | NCT04360265 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Ultragenyx Pharmaceutical Inc | 24 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Hospital Clínico Universitario de Santiago | Santiago de Compostela | Spain | 6 |
| Nationwide Children's Hospital | Columbus | United States | 309 |
| Vall d'Hebron Barcelona Campus | Barcelona | Spain | 1 |
| Women's and Children's Hospital | North Adelaide | Australia | 2 |