Cerliponase Alfa Observational Study in the US
Cerliponase Alfa Observational Study in the US
Active, not recruiting · NCT04476862 · Registry updated 2026-06-30Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Cerliponase Alfa Observational Study in the US | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative disease | Active, not recruiting | Not stated | 2026-06-30 | NCT04476862 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| BioMarin Pharmaceutical | 32 |
16 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Advent Health | Orlando | United States | 14 |
| Arkansas Children's Hospital | Little Rock | United States | 3 |
| Boston Children's Hospital, | Boston | United States | 1 |
| Children's Healthcare of Atlanta | Atlanta | United States | 38 |
| Children's Hospital Minnesota | Minneapolis | United States | 2 |
| Children's Hospital of Colorado | Aurora | United States | 28 |
| Children'S Hospital of Orange County | Orange | United States | 128 |
| Children's National Hospital | Washington D.C. | United States | 100 |
| Mt. Sinai School of Medicine | New York | United States | 5 |
| Nationwide Children's Hospital | Columbus | United States | 1 |
| NYU Langone Medical Center | New York | United States | 1 |
| Rush University Medical Center | Chicago | United States | 283 |
| Seattle Children's Hospital | Seattle | United States | 1 |
| Texas Children's Hospital | Houston | United States | 187 |
| University of Oklahoma Health Sciences Center | Oklahoma City | United States | 491 |
| University of Rochester Medical Center | Rochester | United States | 162 |