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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Programcarnitine-acylcarnitine translocase deficiency, mitochondrial trifunctional protein deficiency, very long chain acyl-CoA dehydrogenase deficiencyActive, not recruitingNot stated2026-06-03NCT04632953

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OrganizationsLinked trials
Ultragenyx Pharmaceutical Inc24

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's HospitalChicagoUnited States8
Boston Children's HospitalBostonUnited States20
CHEO (Children's Hospital Eastern Ontario)OttawaCanada1
Children's Hospital of ColoradoAuroraUnited States28
Children's Hospital of Pittsburgh of UPMCPittsburghUnited States120
Columbia UniversityNew YorkUnited States154
Nationwide Children's HospitalColumbusUnited States309
Phoenix Children's HospitalPhoenixUnited States95
Seattle Children's HospitalSeattleUnited States1
SickKids (The Hospital for Sick Children)TorontoCanada1
The Emory ClinicAtlantaUnited States10
University of AlbertaEdmontonCanada4
University of California San FranciscoSan FranciscoUnited States80
University of MinnesotaMinneapolisUnited States30
University of South FloridaTampaUnited States65
University of UtahSalt Lake CityUnited States72