Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program
Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program
Active, not recruiting · NCT04632953 · Registry updated 2026-06-03Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program | carnitine-acylcarnitine translocase deficiency, mitochondrial trifunctional protein deficiency, very long chain acyl-CoA dehydrogenase deficiency | Active, not recruiting | Not stated | 2026-06-03 | NCT04632953 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Ultragenyx Pharmaceutical Inc | 24 |
16 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital | Chicago | United States | 8 |
| Boston Children's Hospital | Boston | United States | 20 |
| CHEO (Children's Hospital Eastern Ontario) | Ottawa | Canada | 1 |
| Children's Hospital of Colorado | Aurora | United States | 28 |
| Children's Hospital of Pittsburgh of UPMC | Pittsburgh | United States | 120 |
| Columbia University | New York | United States | 154 |
| Nationwide Children's Hospital | Columbus | United States | 309 |
| Phoenix Children's Hospital | Phoenix | United States | 95 |
| Seattle Children's Hospital | Seattle | United States | 1 |
| SickKids (The Hospital for Sick Children) | Toronto | Canada | 1 |
| The Emory Clinic | Atlanta | United States | 10 |
| University of Alberta | Edmonton | Canada | 4 |
| University of California San Francisco | San Francisco | United States | 80 |
| University of Minnesota | Minneapolis | United States | 30 |
| University of South Florida | Tampa | United States | 65 |
| University of Utah | Salt Lake City | United States | 72 |