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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study for the Treatment for CLN7 DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseActive, not recruitingPhase 12025-12-31NCT04737460

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OrganizationsLinked trials
Benjamin Greenberg1

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Research sitesCityCountryLinked trials
Children' HealthDallasUnited States1